Molecular architecture determines brain delivery of a transferrin-receptor targeted lysosomal enzyme
Annie Arguello, Cathal S. Mahon, Meredith E. K. Calvert, Darren Chan, Jason C. Dugas, Michelle E. Pizzo, Elliot R. Thomsen, Roni Chau, Lorna A. Damo, Joseph Duque, Timothy Earr, Meng Fang, Tina Giese, Do Jin Kim, Nicholas Liang, Isabel A. Lopez, Hoang N. Nguyen, Hilda Solanoy, Buyankhishig Tsogtbaatar, Julie C. Ullman, Junhua Wang, Mark S. Dennis, Dolores Diaz, Kannan Gunasekaran, Kirk R. Henne, Joseph W. Lewcock, Pascal E. Sanchez, Matthew D. Troyer, Jeffrey M. Harris, Kimberly Scearce-Levie, Lu Shan, Ryan J. Watts, Robert G. Thorne, Anastasia G. Henry, Mihalis S. Kariolis
bioRxiv 2021.05.21.445035; doi: https://doi.org/10.1101/2021.05.21.445035