Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies
Vigneshwaran Venkatesan, Abisha Crystal Christopher, Prathibha Babu, Manoj Kumar K Azhagiri, Kaivalya Walavalkar, Bharath Saravanan, Saranya Srinivasan, Karthik V Karuppusamy, Annlin Jacob, Sumathi Rangaraj, Abhirup Bagchi, Aswin Anand Pai, Yukio Nakamura, Poonkuzhali Balasubramanian, Rekha Pai, Srujan Kumar Marepally, Kumarasamypet Murugesan Mohankumar, Shaji R Velayudhan, Dimple Notani, Alok Srivastava, Saravanabhavan Thangavel
bioRxiv 2022.07.11.499646; doi: https://doi.org/10.1101/2022.07.11.499646