Online Self-Report Data for Duchenne Muscular Dystrophy confirms natural history and can be used to assess for therapeutic benefits
Richard T. Wang, Cheri Silverstein, J. Wes Ulm, Ivana Jankovic, Ascia Eskin, Ake Lu, Vanessa Rangel Miller, Rita M. Cantor, Ning Li, Robert Elashoff, Ann S. Martin, Holly Peay, Stanley F. Nelson
bioRxiv 012344; doi: https://doi.org/10.1101/012344