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In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
Clara T Nicolas, Caitlin J VanLith, Kari L Allen, Raymond D Hickey, Zeji Du, Lori G Hillin, Rebekah M Guthman, William J Cao, Aditya Bhagwate, Daniel O’Brien, Jean-Pierre Kocher, Robert A Kaiser, Stephen J Russell, Joseph B Lillegard
doi: https://doi.org/10.1101/2021.01.02.425079
Clara T Nicolas
1Department of Surgery, Mayo Clinic, Rochester, MN
2Faculty of Medicine, University of Barcelona, Barcelona, Spain
3Department of Surgery, University of Alabama Birmingham, Birmingham, AL
Caitlin J VanLith
1Department of Surgery, Mayo Clinic, Rochester, MN
Kari L Allen
1Department of Surgery, Mayo Clinic, Rochester, MN
Raymond D Hickey
1Department of Surgery, Mayo Clinic, Rochester, MN
4Department of Molecular Medicine, Mayo Clinic, Rochester, MN
Zeji Du
1Department of Surgery, Mayo Clinic, Rochester, MN
Lori G Hillin
1Department of Surgery, Mayo Clinic, Rochester, MN
Rebekah M Guthman
1Department of Surgery, Mayo Clinic, Rochester, MN
5Medical College of Wisconsin, Wausau, WI
William J Cao
1Department of Surgery, Mayo Clinic, Rochester, MN
Aditya Bhagwate
6Department of Biomedical Statistics and Informatics, Mayo Clinic, Rochester, MN
Daniel O’Brien
6Department of Biomedical Statistics and Informatics, Mayo Clinic, Rochester, MN
Jean-Pierre Kocher
6Department of Biomedical Statistics and Informatics, Mayo Clinic, Rochester, MN
Robert A Kaiser
1Department of Surgery, Mayo Clinic, Rochester, MN
7Midwest Fetal Care Center, Children’s Hospitals and Clinics of Minnesota, Minneapolis, MN
Stephen J Russell
4Department of Molecular Medicine, Mayo Clinic, Rochester, MN
Joseph B Lillegard
1Department of Surgery, Mayo Clinic, Rochester, MN
7Midwest Fetal Care Center, Children’s Hospitals and Clinics of Minnesota, Minneapolis, MN
8Pediatric Surgical Associates, Minneapolis, MN
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Posted January 03, 2021.
In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
Clara T Nicolas, Caitlin J VanLith, Kari L Allen, Raymond D Hickey, Zeji Du, Lori G Hillin, Rebekah M Guthman, William J Cao, Aditya Bhagwate, Daniel O’Brien, Jean-Pierre Kocher, Robert A Kaiser, Stephen J Russell, Joseph B Lillegard
bioRxiv 2021.01.02.425079; doi: https://doi.org/10.1101/2021.01.02.425079
In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
Clara T Nicolas, Caitlin J VanLith, Kari L Allen, Raymond D Hickey, Zeji Du, Lori G Hillin, Rebekah M Guthman, William J Cao, Aditya Bhagwate, Daniel O’Brien, Jean-Pierre Kocher, Robert A Kaiser, Stephen J Russell, Joseph B Lillegard
bioRxiv 2021.01.02.425079; doi: https://doi.org/10.1101/2021.01.02.425079
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