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Human stem cell-based retina-on-chip as new translational model for validation of AAV retinal gene therapy vectors
Kevin Achberger, View ORCID ProfileMadalena Cipriano, Matthias Düchs, Christian Schön, Stefan Michelfelder, Birgit Stierstorfer, Thorsten Lamla, Stefan G. Kauschke, Johanna Chuchuy, Julia Roosz, Lena Mesch, Virginia Cora, Selin Pars, Natalia Pashkovskaia, Serena Corti, Alexander Kleger, Sebastian Kreuz, Udo Maier, Stefan Liebau, View ORCID ProfilePeter Loskill
doi: https://doi.org/10.1101/2021.03.02.433550
Kevin Achberger
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
Madalena Cipriano
2Fraunhofer Institute for Interfacial Engineering and Biotechnology IGB, Nobelstrasse, Stuttgart, Germany
Matthias Düchs
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Christian Schön
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Stefan Michelfelder
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Birgit Stierstorfer
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Thorsten Lamla
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Stefan G. Kauschke
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Johanna Chuchuy
2Fraunhofer Institute for Interfacial Engineering and Biotechnology IGB, Nobelstrasse, Stuttgart, Germany
4Department of Biomedical Sciences, Faculty of Medicine, Eberhard Karls University Tübingen, Tübingen, Germany
Julia Roosz
2Fraunhofer Institute for Interfacial Engineering and Biotechnology IGB, Nobelstrasse, Stuttgart, Germany
Lena Mesch
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
Virginia Cora
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
Selin Pars
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
Natalia Pashkovskaia
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
Serena Corti
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
Alexander Kleger
5Department of Internal Medicine I, University Hospital Ulm, Ulm, Germany
Sebastian Kreuz
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Udo Maier
3Boehringer Ingelheim Pharma GmbH & Co. KG, Biberach an der Riss, Germany
Stefan Liebau
1Institute of Neuroanatomy & Developmental Biology (INDB), Eberhard Karls University Tübingen, Tübingen, Germany
6Center for Neurosensory Systems (ZFN), Eberhard Karls University Tübingen, Tübingen, Germany
Peter Loskill
2Fraunhofer Institute for Interfacial Engineering and Biotechnology IGB, Nobelstrasse, Stuttgart, Germany
4Department of Biomedical Sciences, Faculty of Medicine, Eberhard Karls University Tübingen, Tübingen, Germany
Article usage
Posted March 02, 2021.
Human stem cell-based retina-on-chip as new translational model for validation of AAV retinal gene therapy vectors
Kevin Achberger, Madalena Cipriano, Matthias Düchs, Christian Schön, Stefan Michelfelder, Birgit Stierstorfer, Thorsten Lamla, Stefan G. Kauschke, Johanna Chuchuy, Julia Roosz, Lena Mesch, Virginia Cora, Selin Pars, Natalia Pashkovskaia, Serena Corti, Alexander Kleger, Sebastian Kreuz, Udo Maier, Stefan Liebau, Peter Loskill
bioRxiv 2021.03.02.433550; doi: https://doi.org/10.1101/2021.03.02.433550
Human stem cell-based retina-on-chip as new translational model for validation of AAV retinal gene therapy vectors
Kevin Achberger, Madalena Cipriano, Matthias Düchs, Christian Schön, Stefan Michelfelder, Birgit Stierstorfer, Thorsten Lamla, Stefan G. Kauschke, Johanna Chuchuy, Julia Roosz, Lena Mesch, Virginia Cora, Selin Pars, Natalia Pashkovskaia, Serena Corti, Alexander Kleger, Sebastian Kreuz, Udo Maier, Stefan Liebau, Peter Loskill
bioRxiv 2021.03.02.433550; doi: https://doi.org/10.1101/2021.03.02.433550
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