Characteristics and data reporting of rare disease clinical trials: Getting better but still room for improvement

Nina K. Mair; Jürgen Gottowik; Raul Rodriguez-Esteban; Timothy J. Seabrook

doi:10.1101/2021.12.03.471055

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Characteristics and data reporting of rare disease clinical trials: Getting better but still room for improvement

View ORCID ProfileNina K. Mair, View ORCID ProfileJürgen Gottowik, View ORCID ProfileRaul Rodriguez-Esteban, Timothy J. Seabrook

doi: https://doi.org/10.1101/2021.12.03.471055

Nina K. Mair

1Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd., Basel, Switzerland

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ORCID record for Nina K. Mair
For correspondence: mair.nina@virology.uzh.ch

Jürgen Gottowik

1Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd., Basel, Switzerland

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Raul Rodriguez-Esteban

1Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd., Basel, Switzerland

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Timothy J. Seabrook

1Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, F. Hoffmann-La Roche Ltd., Basel, Switzerland

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Posted December 23, 2021.

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Characteristics and data reporting of rare disease clinical trials: Getting better but still room for improvement

Nina K. Mair, Jürgen Gottowik, Raul Rodriguez-Esteban, Timothy J. Seabrook

bioRxiv 2021.12.03.471055; doi: https://doi.org/10.1101/2021.12.03.471055

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Characteristics and data reporting of rare disease clinical trials: Getting better but still room for improvement

Nina K. Mair, Jürgen Gottowik, Raul Rodriguez-Esteban, Timothy J. Seabrook

bioRxiv 2021.12.03.471055; doi: https://doi.org/10.1101/2021.12.03.471055

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