Skip to main content
bioRxiv
  • Home
  • About
  • Submit
  • ALERTS / RSS
Advanced Search
New Results

Potential limitations of micro-dystrophin gene therapy for Duchenne muscular dystrophy

Cora C. Hart, Young il Lee, Jun Xie, Guangping Gao, David W. Hammers, H. Lee Sweeney
doi: https://doi.org/10.1101/2022.10.02.510519
Cora C. Hart
1Department of Pharmacology & Therapeutics, University of Florida College of Medicine; Gainesville, FL 32610
2Myology Institute, University of Florida College of Medicine; Gainesville, FL 32610
  • Find this author on Google Scholar
  • Find this author on PubMed
  • Search for this author on this site
Young il Lee
1Department of Pharmacology & Therapeutics, University of Florida College of Medicine; Gainesville, FL 32610
2Myology Institute, University of Florida College of Medicine; Gainesville, FL 32610
  • Find this author on Google Scholar
  • Find this author on PubMed
  • Search for this author on this site
Jun Xie
3Horae Gene Therapy Center, University of Massachusetts Medical School, Worchester, MA 01655
  • Find this author on Google Scholar
  • Find this author on PubMed
  • Search for this author on this site
Guangping Gao
3Horae Gene Therapy Center, University of Massachusetts Medical School, Worchester, MA 01655
  • Find this author on Google Scholar
  • Find this author on PubMed
  • Search for this author on this site
David W. Hammers
1Department of Pharmacology & Therapeutics, University of Florida College of Medicine; Gainesville, FL 32610
2Myology Institute, University of Florida College of Medicine; Gainesville, FL 32610
  • Find this author on Google Scholar
  • Find this author on PubMed
  • Search for this author on this site
H. Lee Sweeney
1Department of Pharmacology & Therapeutics, University of Florida College of Medicine; Gainesville, FL 32610
2Myology Institute, University of Florida College of Medicine; Gainesville, FL 32610
  • Find this author on Google Scholar
  • Find this author on PubMed
  • Search for this author on this site
  • For correspondence: lsweeney@ufl.edu
  • Abstract
  • Full Text
  • Info/History
  • Metrics
  • Preview PDF
Loading

Article Information

doi 
https://doi.org/10.1101/2022.10.02.510519
History 
  • October 5, 2022.
Copyright 
The copyright holder for this preprint is the author/funder, who has granted bioRxiv a license to display the preprint in perpetuity. It is made available under a CC-BY-NC-ND 4.0 International license.

Author Information

  1. Cora C. Hart1,2,4,
  2. Young il Lee1,2,4,
  3. Jun Xie3,
  4. Guangping Gao3,
  5. David W. Hammers1,2,5 and
  6. H. Lee Sweeney1,2,5,*
  1. 1Department of Pharmacology & Therapeutics, University of Florida College of Medicine; Gainesville, FL 32610
  2. 2Myology Institute, University of Florida College of Medicine; Gainesville, FL 32610
  3. 3Horae Gene Therapy Center, University of Massachusetts Medical School, Worchester, MA 01655
  1. ↵*Corresponding author Correspondence:
    H. Lee Sweeney, 1200 Newell Dr. ARB R5-216, Gainesville, FL 32610-0267, Phone: 352-273-9416, Fax: 352-392-3558, Email: lsweeney{at}ufl.edu
  1. ↵4 Equal contributions by these authors;

  2. ↵5 Equal contributions by these authors;

Back to top
PreviousNext
Posted October 05, 2022.
Download PDF
Email

Thank you for your interest in spreading the word about bioRxiv.

NOTE: Your email address is requested solely to identify you as the sender of this article.

Enter multiple addresses on separate lines or separate them with commas.
Potential limitations of micro-dystrophin gene therapy for Duchenne muscular dystrophy
(Your Name) has forwarded a page to you from bioRxiv
(Your Name) thought you would like to see this page from the bioRxiv website.
CAPTCHA
This question is for testing whether or not you are a human visitor and to prevent automated spam submissions.
Share
Potential limitations of micro-dystrophin gene therapy for Duchenne muscular dystrophy
Cora C. Hart, Young il Lee, Jun Xie, Guangping Gao, David W. Hammers, H. Lee Sweeney
bioRxiv 2022.10.02.510519; doi: https://doi.org/10.1101/2022.10.02.510519
Reddit logo Twitter logo Facebook logo LinkedIn logo Mendeley logo
Citation Tools
Potential limitations of micro-dystrophin gene therapy for Duchenne muscular dystrophy
Cora C. Hart, Young il Lee, Jun Xie, Guangping Gao, David W. Hammers, H. Lee Sweeney
bioRxiv 2022.10.02.510519; doi: https://doi.org/10.1101/2022.10.02.510519

Citation Manager Formats

  • BibTeX
  • Bookends
  • EasyBib
  • EndNote (tagged)
  • EndNote 8 (xml)
  • Medlars
  • Mendeley
  • Papers
  • RefWorks Tagged
  • Ref Manager
  • RIS
  • Zotero
  • Tweet Widget
  • Facebook Like
  • Google Plus One

Subject Area

  • Pharmacology and Toxicology
Subject Areas
All Articles
  • Animal Behavior and Cognition (4235)
  • Biochemistry (9136)
  • Bioengineering (6784)
  • Bioinformatics (24001)
  • Biophysics (12129)
  • Cancer Biology (9534)
  • Cell Biology (13778)
  • Clinical Trials (138)
  • Developmental Biology (7636)
  • Ecology (11702)
  • Epidemiology (2066)
  • Evolutionary Biology (15513)
  • Genetics (10644)
  • Genomics (14327)
  • Immunology (9483)
  • Microbiology (22841)
  • Molecular Biology (9090)
  • Neuroscience (48995)
  • Paleontology (355)
  • Pathology (1482)
  • Pharmacology and Toxicology (2570)
  • Physiology (3846)
  • Plant Biology (8331)
  • Scientific Communication and Education (1471)
  • Synthetic Biology (2296)
  • Systems Biology (6192)
  • Zoology (1301)