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Genetic deletion of the inflammation-regulated microRNA miR-146a increases exon-skipping mediated dystrophin restoration in Duchenne muscular dystrophy
View ORCID ProfileNikki M. McCormack, Kelsey A. Calabrese, View ORCID ProfileChristopher B. Tully, View ORCID ProfileChristopher R. Heier, View ORCID ProfileAlyson A. Fiorillo
doi: https://doi.org/10.1101/2023.05.09.540042
Nikki M. McCormack
1Center for Genetic Medicine Research, Children’s National Hospital, Washington, District of Columbia, USA
Kelsey A. Calabrese
1Center for Genetic Medicine Research, Children’s National Hospital, Washington, District of Columbia, USA
Christopher B. Tully
1Center for Genetic Medicine Research, Children’s National Hospital, Washington, District of Columbia, USA
Christopher R. Heier
1Center for Genetic Medicine Research, Children’s National Hospital, Washington, District of Columbia, USA
2Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, District of Columbia, USA
Alyson A. Fiorillo
1Center for Genetic Medicine Research, Children’s National Hospital, Washington, District of Columbia, USA
2Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, District of Columbia, USA
Posted May 09, 2023.
Genetic deletion of the inflammation-regulated microRNA miR-146a increases exon-skipping mediated dystrophin restoration in Duchenne muscular dystrophy
Nikki M. McCormack, Kelsey A. Calabrese, Christopher B. Tully, Christopher R. Heier, Alyson A. Fiorillo
bioRxiv 2023.05.09.540042; doi: https://doi.org/10.1101/2023.05.09.540042
Genetic deletion of the inflammation-regulated microRNA miR-146a increases exon-skipping mediated dystrophin restoration in Duchenne muscular dystrophy
Nikki M. McCormack, Kelsey A. Calabrese, Christopher B. Tully, Christopher R. Heier, Alyson A. Fiorillo
bioRxiv 2023.05.09.540042; doi: https://doi.org/10.1101/2023.05.09.540042
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