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Disease exacerbation by fibroblast inclusion in Duchenne Muscular Dystrophy MYOrganoids reveals limitations of microdystrophin therapeutic efficacy
View ORCID ProfileLaura Palmieri, Louna Pili, Abbass Jaber, Ai Vu Hong, Matteo Marcello, Riyad El-Khoury, Guy Brochiet, Anne Bigot, David Israeli, Isabelle Richard, Sonia Albini
doi: https://doi.org/10.1101/2023.07.26.550063
Laura Palmieri
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Louna Pili
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Abbass Jaber
Ai Vu Hong
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Matteo Marcello
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Riyad El-Khoury
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
3Institut de Myologie, Neuromuscular Morphology Unit, Groupe Hospitalier Pitié-Salpêtrière, Paris, France
Guy Brochiet
3Institut de Myologie, Neuromuscular Morphology Unit, Groupe Hospitalier Pitié-Salpêtrière, Paris, France
4AP-HP, Centre de Référence de Pathologie Neuromusculaire Nord/Est/Ile de France, Groupe Hospitalier Pitié-Salpêtrière, Paris, France
Anne Bigot
5Sorbonne Université, Inserm, Institut de Myologie, Centre de Recherche en Myologie, F-75013 Paris, France
David Israeli
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Isabelle Richard
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Sonia Albini
1Genethon, 91100 Evry, France
2Université Paris-Saclay, Univ Evry, Inserm, Généthon, Integrare research unit UMR_S951, 91000, Evry, France
Copyright
The copyright holder for this preprint is the author/funder, who has granted bioRxiv a license to display the preprint in perpetuity. It is made available under a CC-BY-NC-ND 4.0 International license.
Posted November 18, 2024.
Disease exacerbation by fibroblast inclusion in Duchenne Muscular Dystrophy MYOrganoids reveals limitations of microdystrophin therapeutic efficacy
Laura Palmieri, Louna Pili, Abbass Jaber, Ai Vu Hong, Matteo Marcello, Riyad El-Khoury, Guy Brochiet, Anne Bigot, David Israeli, Isabelle Richard, Sonia Albini
bioRxiv 2023.07.26.550063; doi: https://doi.org/10.1101/2023.07.26.550063
Disease exacerbation by fibroblast inclusion in Duchenne Muscular Dystrophy MYOrganoids reveals limitations of microdystrophin therapeutic efficacy
Laura Palmieri, Louna Pili, Abbass Jaber, Ai Vu Hong, Matteo Marcello, Riyad El-Khoury, Guy Brochiet, Anne Bigot, David Israeli, Isabelle Richard, Sonia Albini
bioRxiv 2023.07.26.550063; doi: https://doi.org/10.1101/2023.07.26.550063
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