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Allele-specific silencing of a dominant SETX mutation in familial amyotrophic lateral sclerosis type 4
Audrey Winkelsas, Athena Apfel, Brian Johnson, George Harmison, Dongjun Li, Vivian Cheung, View ORCID ProfileChristopher Grunseich
doi: https://doi.org/10.1101/2024.10.11.617871
Audrey Winkelsas
1National Institute of Neurological Disorders and Stroke, National Institutes of Health, 35 Convent Dr., Bethesda, MD 20892, USA
Athena Apfel
1National Institute of Neurological Disorders and Stroke, National Institutes of Health, 35 Convent Dr., Bethesda, MD 20892, USA
Brian Johnson
1National Institute of Neurological Disorders and Stroke, National Institutes of Health, 35 Convent Dr., Bethesda, MD 20892, USA
George Harmison
1National Institute of Neurological Disorders and Stroke, National Institutes of Health, 35 Convent Dr., Bethesda, MD 20892, USA
Dongjun Li
2Department of Pediatrics and Life Sciences Institute, University of Michigan, 210 Washtenaw, Ann Arbor, MI 48109, USA
Vivian Cheung
2Department of Pediatrics and Life Sciences Institute, University of Michigan, 210 Washtenaw, Ann Arbor, MI 48109, USA
Christopher Grunseich
1National Institute of Neurological Disorders and Stroke, National Institutes of Health, 35 Convent Dr., Bethesda, MD 20892, USA

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Posted October 12, 2024.
Allele-specific silencing of a dominant SETX mutation in familial amyotrophic lateral sclerosis type 4
Audrey Winkelsas, Athena Apfel, Brian Johnson, George Harmison, Dongjun Li, Vivian Cheung, Christopher Grunseich
bioRxiv 2024.10.11.617871; doi: https://doi.org/10.1101/2024.10.11.617871
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