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CRISPR-Cas9 generated Pompe knock-in murine model exhibits early-onset cardiomyopathy and impaired skeletal muscle function
Jeffrey Y. Huang, Shih-Hsin Kan, Anthony D. Rangel, Yunghang Chan, Jeremy Davis-Turak, Nancy D. Dalton, Jon Neumann, Raymond Y. Wang
doi: https://doi.org/10.1101/780320
Jeffrey Y. Huang
1CHOC Children’s Research Institute, Orange, CA 92868
Shih-Hsin Kan
1CHOC Children’s Research Institute, Orange, CA 92868
Anthony D. Rangel
1CHOC Children’s Research Institute, Orange, CA 92868
Yunghang Chan
2Department of Medicine, University of California San Diego, La Jolla, CA 92093
Jeremy Davis-Turak
3OnRamp BioInformatics, Inc. San Diego, CA 92121
Nancy D. Dalton
2Department of Medicine, University of California San Diego, La Jolla, CA 92093
Jon Neumann
4Transgenic Mouse Facility, University of California Irvine, Irvine, CA 92697
Raymond Y. Wang
1CHOC Children’s Research Institute, Orange, CA 92868
5Department of Pediatrics, University of California-Irvine School of Medicine, Irvine CA 92697
6Division of Metabolic Disorders, CHOC Children’s Specialists, Orange, CA 92868
Posted September 24, 2019.
CRISPR-Cas9 generated Pompe knock-in murine model exhibits early-onset cardiomyopathy and impaired skeletal muscle function
Jeffrey Y. Huang, Shih-Hsin Kan, Anthony D. Rangel, Yunghang Chan, Jeremy Davis-Turak, Nancy D. Dalton, Jon Neumann, Raymond Y. Wang
bioRxiv 780320; doi: https://doi.org/10.1101/780320
CRISPR-Cas9 generated Pompe knock-in murine model exhibits early-onset cardiomyopathy and impaired skeletal muscle function
Jeffrey Y. Huang, Shih-Hsin Kan, Anthony D. Rangel, Yunghang Chan, Jeremy Davis-Turak, Nancy D. Dalton, Jon Neumann, Raymond Y. Wang
bioRxiv 780320; doi: https://doi.org/10.1101/780320
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