New Results
Human iPSC modeling elucidates mutation-specific responses to gene therapy in a genotypically diverse dominant maculopathy
Divya Sinha, View ORCID ProfileBenjamin Steyer, Pawan K. Shahi, Katherine Mueller, Rasa Valiauga, Kimberly L. Edwards, Cole Bacig, Stephanie S. Steltzer, Sandhya Srinivasan, Amr Abdeen, Evan Cory, Viswesh Periyasamy, Alireza Fotuhi Siahpirani, Sushmita Roy, Bikash R. Pattnaik, View ORCID ProfileKrishanu Saha, David M. Gamm
doi: https://doi.org/10.1101/796581
Divya Sinha
1McPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA
2Waisman Center, University of Wisconsin-Madison, Madison, WI, USA
Benjamin Steyer
1McPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Pawan K. Shahi
1McPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA
4Department of Pediatrics, University of Wisconsin-Madison, Madison, WI, USA
Katherine Mueller
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Rasa Valiauga
2Waisman Center, University of Wisconsin-Madison, Madison, WI, USA
Kimberly L. Edwards
2Waisman Center, University of Wisconsin-Madison, Madison, WI, USA
Cole Bacig
2Waisman Center, University of Wisconsin-Madison, Madison, WI, USA
Stephanie S. Steltzer
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Sandhya Srinivasan
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Amr Abdeen
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Evan Cory
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Viswesh Periyasamy
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Alireza Fotuhi Siahpirani
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
Sushmita Roy
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
5Department of Biostatistics, University of Wisconsin-Madison, Madison, WI, USA
Bikash R. Pattnaik
1McPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA
4Department of Pediatrics, University of Wisconsin-Madison, Madison, WI, USA
6Department of Ophthalmology and Visual Sciences, University of Wisconsin-Madison, Madison, WI, USA
Krishanu Saha
1McPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA
3Wisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA
7Department of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI, USA
David M. Gamm
1McPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA
2Waisman Center, University of Wisconsin-Madison, Madison, WI, USA
6Department of Ophthalmology and Visual Sciences, University of Wisconsin-Madison, Madison, WI, USA
Article usage
Posted October 10, 2019.
Human iPSC modeling elucidates mutation-specific responses to gene therapy in a genotypically diverse dominant maculopathy
Divya Sinha, Benjamin Steyer, Pawan K. Shahi, Katherine Mueller, Rasa Valiauga, Kimberly L. Edwards, Cole Bacig, Stephanie S. Steltzer, Sandhya Srinivasan, Amr Abdeen, Evan Cory, Viswesh Periyasamy, Alireza Fotuhi Siahpirani, Sushmita Roy, Bikash R. Pattnaik, Krishanu Saha, David M. Gamm
bioRxiv 796581; doi: https://doi.org/10.1101/796581
Human iPSC modeling elucidates mutation-specific responses to gene therapy in a genotypically diverse dominant maculopathy
Divya Sinha, Benjamin Steyer, Pawan K. Shahi, Katherine Mueller, Rasa Valiauga, Kimberly L. Edwards, Cole Bacig, Stephanie S. Steltzer, Sandhya Srinivasan, Amr Abdeen, Evan Cory, Viswesh Periyasamy, Alireza Fotuhi Siahpirani, Sushmita Roy, Bikash R. Pattnaik, Krishanu Saha, David M. Gamm
bioRxiv 796581; doi: https://doi.org/10.1101/796581
Subject Area
Subject Areas
- Biochemistry (11739)
- Bioengineering (8750)
- Bioinformatics (29189)
- Biophysics (14967)
- Cancer Biology (12093)
- Cell Biology (17409)
- Clinical Trials (138)
- Developmental Biology (9419)
- Ecology (14178)
- Epidemiology (2067)
- Evolutionary Biology (18301)
- Genetics (12238)
- Genomics (16797)
- Immunology (11865)
- Microbiology (28068)
- Molecular Biology (11583)
- Neuroscience (60953)
- Paleontology (451)
- Pathology (1870)
- Pharmacology and Toxicology (3238)
- Physiology (4957)
- Plant Biology (10425)
- Synthetic Biology (2884)
- Systems Biology (7338)
- Zoology (1651)