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Human iPSC modeling reveals mutation-specific responses to gene therapy in Best disease
Divya Sinha, View ORCID ProfileBenjamin Steyer, Pawan K. Shahi, Katherine Mueller, Rasa Valiauga, Kimberly L. Edwards, Cole Bacig, Stephanie S. Steltzer, Sandhya Srinivasan, Amr Abdeen, Evan Cory, Viswesh Periyasamy, Alireza Fotuhi Siahpirani, Edwin M. Stone, Budd A Tucker, Sushmita Roy, Bikash R. Pattnaik, View ORCID ProfileKrishanu Saha, David M. Gamm
doi: https://doi.org/10.1101/796581
Divya Sinha
aMcPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA 53705
bWaisman Center, University of Wisconsin-Madison, Madison, WI, USA 53705
Benjamin Steyer
aMcPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA 53705
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Pawan K. Shahi
aMcPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA 53705
dDepartment of Pediatrics, University of Wisconsin-Madison, Madison, WI, USA 53792
Katherine Mueller
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Rasa Valiauga
bWaisman Center, University of Wisconsin-Madison, Madison, WI, USA 53705
Kimberly L. Edwards
bWaisman Center, University of Wisconsin-Madison, Madison, WI, USA 53705
Cole Bacig
bWaisman Center, University of Wisconsin-Madison, Madison, WI, USA 53705
Stephanie S. Steltzer
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Sandhya Srinivasan
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Amr Abdeen
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Evan Cory
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Viswesh Periyasamy
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Alireza Fotuhi Siahpirani
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
Edwin M. Stone
eDepartment of Ophthalmology and Visual Sciences, Carver College of Medicine, Iowa City, IA 52242
Budd A Tucker
eDepartment of Ophthalmology and Visual Sciences, Carver College of Medicine, Iowa City, IA 52242
Sushmita Roy
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
fDepartment of Biostatistics, University of Wisconsin-Madison, Madison, WI, USA 53792
Bikash R. Pattnaik
aMcPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA 53705
dDepartment of Pediatrics, University of Wisconsin-Madison, Madison, WI, USA 53792
gDepartment of Ophthalmology and Visual Sciences, University of Wisconsin-Madison, Madison, WI, USA 53705
Krishanu Saha
aMcPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA 53705
cWisconsin Institute for Discovery, University of Wisconsin-Madison, Madison, WI, USA 53715
hDepartment of Biomedical Engineering, University of Wisconsin-Madison, Madison, WI, USA 53706
David M. Gamm
aMcPherson Eye Research Institute, University of Wisconsin-Madison, Madison, WI, USA 53705
bWaisman Center, University of Wisconsin-Madison, Madison, WI, USA 53705
gDepartment of Ophthalmology and Visual Sciences, University of Wisconsin-Madison, Madison, WI, USA 53705
Posted January 30, 2020.
Human iPSC modeling reveals mutation-specific responses to gene therapy in Best disease
Divya Sinha, Benjamin Steyer, Pawan K. Shahi, Katherine Mueller, Rasa Valiauga, Kimberly L. Edwards, Cole Bacig, Stephanie S. Steltzer, Sandhya Srinivasan, Amr Abdeen, Evan Cory, Viswesh Periyasamy, Alireza Fotuhi Siahpirani, Edwin M. Stone, Budd A Tucker, Sushmita Roy, Bikash R. Pattnaik, Krishanu Saha, David M. Gamm
bioRxiv 796581; doi: https://doi.org/10.1101/796581
Human iPSC modeling reveals mutation-specific responses to gene therapy in Best disease
Divya Sinha, Benjamin Steyer, Pawan K. Shahi, Katherine Mueller, Rasa Valiauga, Kimberly L. Edwards, Cole Bacig, Stephanie S. Steltzer, Sandhya Srinivasan, Amr Abdeen, Evan Cory, Viswesh Periyasamy, Alireza Fotuhi Siahpirani, Edwin M. Stone, Budd A Tucker, Sushmita Roy, Bikash R. Pattnaik, Krishanu Saha, David M. Gamm
bioRxiv 796581; doi: https://doi.org/10.1101/796581
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