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Gene augmentation and read-through rescue channelopathy in an iPSC-RPE model of congenital blindness
Pawan K. Shahi, Dalton Hermans, Divya Sinha, Simran Brar, Hannah Moulton, Sabrina Stulo, Katarzyna D. Borys, Elizabeth Capowski, De-Ann M. Pillers, David M. Gamm, View ORCID ProfileBikash. R. Pattnaik
doi: https://doi.org/10.1101/485847
Pawan K. Shahi
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
2McPherson Eye Research, University of Wisconsin-Madison, Madison
Dalton Hermans
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
Divya Sinha
2McPherson Eye Research, University of Wisconsin-Madison, Madison
3Waisman Center, University of Wisconsin-Madison, Madison
Simran Brar
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
Hannah Moulton
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
Sabrina Stulo
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
Katarzyna D. Borys
3Waisman Center, University of Wisconsin-Madison, Madison
Elizabeth Capowski
2McPherson Eye Research, University of Wisconsin-Madison, Madison
3Waisman Center, University of Wisconsin-Madison, Madison
De-Ann M. Pillers
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
2McPherson Eye Research, University of Wisconsin-Madison, Madison
4Medical Genetics, University of Wisconsin-Madison, Madison
David M. Gamm
2McPherson Eye Research, University of Wisconsin-Madison, Madison
3Waisman Center, University of Wisconsin-Madison, Madison
5Department of Ophthalmology and Visual Sciences, University of Wisconsin-Madison.
Bikash. R. Pattnaik
1Division of Neonatology, Department of Pediatrics, University of Wisconsin-Madison, Madison
2McPherson Eye Research, University of Wisconsin-Madison, Madison
5Department of Ophthalmology and Visual Sciences, University of Wisconsin-Madison.
Article usage
Posted December 04, 2018.
Gene augmentation and read-through rescue channelopathy in an iPSC-RPE model of congenital blindness
Pawan K. Shahi, Dalton Hermans, Divya Sinha, Simran Brar, Hannah Moulton, Sabrina Stulo, Katarzyna D. Borys, Elizabeth Capowski, De-Ann M. Pillers, David M. Gamm, Bikash. R. Pattnaik
bioRxiv 485847; doi: https://doi.org/10.1101/485847
Gene augmentation and read-through rescue channelopathy in an iPSC-RPE model of congenital blindness
Pawan K. Shahi, Dalton Hermans, Divya Sinha, Simran Brar, Hannah Moulton, Sabrina Stulo, Katarzyna D. Borys, Elizabeth Capowski, De-Ann M. Pillers, David M. Gamm, Bikash. R. Pattnaik
bioRxiv 485847; doi: https://doi.org/10.1101/485847
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