Small molecule antagonists of Tcf4/beta-catenin complex inhibit the growth of HCC cells in vitro and in vivo

Int J Cancer. 2010 May 15;126(10):2426-36. doi: 10.1002/ijc.24810.

Abstract

Hepatocellular carcinoma (HCC) is the 5th most common cancer worldwide. It is intrinsically resistant toward standard chemotherapy, making it imperative to develop novel selective chemotherapeutic agents. The Wnt/beta-catenin pathway plays critical roles in development and oncogenesis, and is dysregulated in HCC. Our study aims to evaluate the activity of 3 small molecule antagonists of the Tcf4/beta-catenin complex (PKF118-310, PKF115-584 and CGP049090) on HCC cell lines in vitro and in vivo. All 3 chemicals displayed dose-dependent cytotoxicity in vitro against all 3 HCC cell lines (HepG2, Hep40 and Huh7), but were at least 10 times less cytotoxic to normal hepatocytes (from 3 donors) by using ATP assay. In HepG2 and Huh7 cells, treatment with the antagonists decreased Tcf4/beta-catenin binding capability and transcriptional activity, associated with downregulation of the endogenous Tcf4/ beta-catenin target genes c-Myc, cyclin D1 and survivin. In HepG2 and Huh7 cells, treatment with the antagonists induced apoptosis and cell cycle arrest at the G1/S phase. All antagonists suppressed in vivo tumor growth in a HepG2 xenograft model, associated with apoptosis and reduced c-Myc, cyclin D1 and survivin expressions. Our results suggest that these 3 antagonists of the Tcf4/beta-catenin complex are potential chemotherapeutic agents which may offer a pathway specific option for the clinical management of HCC.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antineoplastic Agents / pharmacology*
  • Apoptosis / drug effects
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors / drug effects
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors / metabolism*
  • Blotting, Western
  • Carcinoma, Hepatocellular / drug therapy*
  • Carcinoma, Hepatocellular / metabolism
  • Cell Line, Tumor
  • Cyclin D1 / drug effects
  • Dose-Response Relationship, Drug
  • Down-Regulation / drug effects
  • Drug Screening Assays, Antitumor
  • Gene Expression Regulation, Neoplastic / drug effects
  • Genes, myc / drug effects
  • Hepatocytes / drug effects
  • Hepatocytes / metabolism
  • Humans
  • Immunohistochemistry
  • Inhibitor of Apoptosis Proteins
  • Liver Neoplasms / drug therapy*
  • Liver Neoplasms / metabolism
  • Mice
  • Mice, Nude
  • Microtubule-Associated Proteins / drug effects
  • Perylene / analogs & derivatives
  • Perylene / pharmacology
  • Pyrimidinones / pharmacology
  • Random Allocation
  • Signal Transduction / drug effects
  • Survivin
  • Transcription Factor 4
  • Transcription Factors / drug effects
  • Transcription Factors / metabolism*
  • Triazines / pharmacology
  • Wnt Proteins / metabolism
  • Xenograft Model Antitumor Assays
  • beta Catenin / drug effects
  • beta Catenin / metabolism*

Substances

  • Antineoplastic Agents
  • BIRC5 protein, human
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors
  • CGP049090
  • Inhibitor of Apoptosis Proteins
  • Microtubule-Associated Proteins
  • PKF115-584
  • PKF118-310
  • Pyrimidinones
  • Survivin
  • TCF4 protein, human
  • Transcription Factor 4
  • Transcription Factors
  • Triazines
  • Wnt Proteins
  • beta Catenin
  • Cyclin D1
  • Perylene