No abstract available
MeSH terms
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Animals
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Drug Discovery / methods
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Drug Discovery / trends*
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Humans
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Muscular Atrophy, Spinal / diagnosis
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Muscular Atrophy, Spinal / drug therapy*
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Muscular Atrophy, Spinal / physiopathology
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Oligonucleotides / therapeutic use*
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Oligonucleotides, Antisense / therapeutic use*
Substances
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Oligonucleotides
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Oligonucleotides, Antisense
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nusinersen