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Efficient Correction of the Sickle Mutation in Human Hematopoietic Stem Cells Using a Cas9 Ribonucleoprotein Complex
Mark A. DeWitt, Wendy Magis, Nicolas L. Bray, Tianjiao Wang, Jennifer R. Berman, Fabrizia Urbinati, Denise P. Muñoz, Donald B. Kohn, Mark C. Walters, Dana Carroll, David K. Martin, Jacob E. Corn
doi: https://doi.org/10.1101/036236
Mark A. DeWitt
1Innovative Genomics Initiative, University of California-Berkeley, CA, USA
2Department of Molecular and Cellular Biology, University of California-Berkeley, CA, USA
Wendy Magis
3Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, California, USA
Nicolas L. Bray
1Innovative Genomics Initiative, University of California-Berkeley, CA, USA
2Department of Molecular and Cellular Biology, University of California-Berkeley, CA, USA
Tianjiao Wang
1Innovative Genomics Initiative, University of California-Berkeley, CA, USA
2Department of Molecular and Cellular Biology, University of California-Berkeley, CA, USA
Jennifer R. Berman
4Digital Biology Center, Bio-Rad Laboratories, Pleasanton, CA, USA.
Fabrizia Urbinati
5Department of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, Los Angeles, CA, USA
Denise P. Muñoz
3Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, California, USA
Donald B. Kohn
5Department of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, Los Angeles, CA, USA
Mark C. Walters
3Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, California, USA
6Blood & Marrow Program, Division of Hematology/Oncology/BMT, UCSF Benioff Children’s Hospital, Oakland, Oakland, CA, USA
Dana Carroll
1Innovative Genomics Initiative, University of California-Berkeley, CA, USA
7Department of Biochemistry, University of Utah School of Medicine, Salt Lake City, Utah, USA
David K. Martin
3Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, California, USA
Jacob E. Corn
1Innovative Genomics Initiative, University of California-Berkeley, CA, USA
2Department of Molecular and Cellular Biology, University of California-Berkeley, CA, USA

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Posted January 15, 2016.
Efficient Correction of the Sickle Mutation in Human Hematopoietic Stem Cells Using a Cas9 Ribonucleoprotein Complex
Mark A. DeWitt, Wendy Magis, Nicolas L. Bray, Tianjiao Wang, Jennifer R. Berman, Fabrizia Urbinati, Denise P. Muñoz, Donald B. Kohn, Mark C. Walters, Dana Carroll, David K. Martin, Jacob E. Corn
bioRxiv 036236; doi: https://doi.org/10.1101/036236
Efficient Correction of the Sickle Mutation in Human Hematopoietic Stem Cells Using a Cas9 Ribonucleoprotein Complex
Mark A. DeWitt, Wendy Magis, Nicolas L. Bray, Tianjiao Wang, Jennifer R. Berman, Fabrizia Urbinati, Denise P. Muñoz, Donald B. Kohn, Mark C. Walters, Dana Carroll, David K. Martin, Jacob E. Corn
bioRxiv 036236; doi: https://doi.org/10.1101/036236
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